Developing drugs for pediatricrare diseases. The company focuses on discovering the genetic basis for diseases and develops drugs that can intervene in the affected pathways.

Advanced medicines for pediatric and rare diseases.

Sector: Healthcare
Sub Sector: Small Molecule (Chemical Entity) Therapeutics & Formulation
Industry: Healthcare
Status: Active
County: Delaware

Contact Information

Neil Inala


Greg Lumpkin


Hakon Hakonarson

Chief Scientific Officer

Sam Inala

VP of Engineering